July 14, 2021

Adrenoleukodystrophy: Advancements in the Care of Children with a Rare Disease

Bradley Miller, MD, PhD
Professor & Division Director
Division of Pediatric Endocrinology
Department of Pediatrics
University of Minnesota

Paul Orchard, MD
Professor
Division of Pediatric Blood and Marrow Transplant & Cellular Therapy
Department of Pediatrics
University of Minnesota

Objectives:
Upon completion of the activity, participants should be better able to:
1. Understand the rationale and interpretation of results for newborn screening in Adrenoleukodystrophy.
2. Describe treatment options for cerebral Adrenoleukodystrophy.
3. Recognize the components necessary for capturing and reporting natural history and treatment outcomes in children with a rare disease.

*For more information about the University of Minnesota's Pediatric Grand Rounds, click here: https://med.umn.edu/pediatrics/pediatric-grand-rounds.

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