"Gene Therapy for Blood Cell Diseases", by Donald B. Kohn, MD

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Gene Therapy for Blood Cell Diseases

Donald B. Kohn, MD

Distinguished Professor

Microbiology, Immunology & Molecular Genetics

Pediatrics (Hematology/Oncology)

Molecular & Medical Pharmacology

University of California, Los Angeles

Objectives:

Upon completion of the activity, participants should be better able to:

Understand the advantages and disadvantages of using gene therapy for blood cell diseases, compared to bone marrow transplant from a donor.
Understand the challenges in advancing gene therapy to clinical trials and FDA approval

*For more information about the University of Minnesota's Pediatric Grand Rounds, click here: https://med.umn.edu/pediatrics/pediatric-grand-rounds